WeCareJourney’s founder Edmund was invited to participate at the recent World Orphan Drug Congress USA (“WODC USA”) 2019. The WODC USA focuses on the most pressing challenges and opportunities to bring rare disease therapies to patients faster, and brings together a global gathering of 1,200 leaders in orphan drugs from 50 countries, featuring over 135 presentations covering all aspects of orphan drug development and rare disease research.
Here are some of his takeaways from WODC USA.
I hope this helps everyone get some insights and that you find it useful.
This will be the start of a series where we aim to help everyone by sharing what we learn, to build capacity and empower others in the SMA and rare disease community.
It is an overview as it is hard to compress 3 days of intense activity across so many presentations, roundtables, and meetups crossing clinical development and regulatory, commercial, rare disease advocacy, global market and patient access, pricing and reimbursement, advanced therapies - clinical, and rare oncology.
If anyone wants to find our more just reach out to me.
Edmund
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